Health Tip on New Treatment that Shows Promise in Niemann-Pick Type C Disorder - Health Tips

Niemann Pick Disease Type C - Symptoms, Causes, Treatment

Lipid trafficking defects in Niemann-Pick type C disease

National Niemann-Pick Disease Foundation, Inc. - October is Global Niemann- Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to the NNPDF go to www.nnpdf.org. #niemannpick #ASMD #

Miglustat in Niemann-Pick disease type C patients: a review, Orphanet Journal of Rare Diseases

5 Most Promising Companies offering hope to patients with Niemann-Pick Type C

Revista de Pediatria SOPERJ

IJMS, Free Full-Text

Niemann-Pick type C disease is associated with mtDNA disorganization.

Main therapies and point of action in Niemann type C disease.

Meet Parker and Woodrow, two AZ children with a rare disease