A hopeful therapy for Niemann-Pick C diseases - The Lancet
Por um escritor misterioso
Last updated 22 fevereiro 2025
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Improved systemic AAV gene therapy with a neurotrophic capsid in
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A hopeful therapy for Niemann-Pick C diseases - The Lancet
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Potential pharmacological strategies targeting the Niemann-Pick C1
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Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological
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Therapeutic intervention for Niemann–Pick type C disease must
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Families plead with FDA for drug to treat Niemann-Pick Disease Type C
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Targeting the central nervous system in lysosomal storage diseases
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Pharmaceuticals, Free Full-Text
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Cost-effectiveness of miglustat versus symptomatic therapy of
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A first therapy for Niemann-Pick C - The Lancet Neurology
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PDF) Niemann-Pick disease treatment: A systematic review of
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Enzyme-replacement therapy for metabolic storage disorders - The
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Experimental treatment for Niemann-Pick disease type C1 appears
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Clinical applications of gene therapy for rare diseases: A review
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Improved systemic AAV gene therapy with a neurotrophic capsid in
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