Potential treatment for Niemann-Pick type C, a rare neurodegenerative disease

Researchers in Japan have improved a potential treatment for a rare genetic disease, decreasing its negative toxic effects by threading it onto a dumb-bell-shaped chain and holding it in place until it reaches its target.

Niemann–Pick Disease Type C

Imaging of neuroinflammation in adult Niemann-Pick type C disease

Niemann–Pick Disease Type C: Induced Pluripotent Stem Cell–Derived

Diagnostic workup and management of patients with suspected

Lipid trafficking defects in Niemann-Pick type C disease

The Neuropsychiatry of Niemann-Pick Type C Disease in Adulthood

Niemann-Pick disease type C

5 Most Promising Companies offering hope to patients with Niemann

Potential treatment for Niemann-Pick type C, a rare

Oxidative Stress: A Pathogenic Mechanism for Niemann-Pick Type C

Niemann-Pick Disease Concise Medical Knowledge

Niemann-Pick type C: contemporary diagnosis and treatment of a