CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular Therapy - Nucleic Acids

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Last updated 04 junho 2024
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
CRISPR/Cas9-mediated A4GALT suppression rescues Fabry disease
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
IJMS, Free Full-Text
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Melatonin Repairs Osteoporotic Bone Defects in Iron-Overloaded
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
PDF) Modelling autosomal dominant optic atrophy associated with
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
PDF) Modelling autosomal dominant optic atrophy associated with
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Functional genomics and the future of iPSCs in disease modeling
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Biomedicines, Free Full-Text
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
CRISPR/Cas9-mediated A4GALT suppression rescues Fabry disease
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Characterisation of a novel OPA1 splice variant resulting in
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular  Therapy - Nucleic Acids
Gene regulation analysis of patient-derived iPSCs and its CRISPR

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