Parents of kids with Niemann Pick C advocate for adrabetadex

Parents of children with Niemann Pick Type C, NPC, hope a company is willing to manufacture adrabetadex, which they say helps their kids.

Community News – NNPDF

In the news: Brave Mum of 3 children with Niemann-Pick disease type C

January – February 2022 Newsletter – NNPDF

Niemann Pick i Norge

January 2021 – NNPDF

Jill Beirl – NNPDF

Families plead with FDA for drug to treat Niemann-Pick Disease Type C

September 2020 – NNPDF

A terrible disease, children at risk, and a promising treatment that's about to vanish: Part II

APMRF Fall Newsletter by parseghianfund - Issuu