Niemann Pick Disease (Nafisa Nawal Islam)

A new regulatory mechanism of STARD1 in Niemann-Pick disease type C (NPC), discovered

Miglustat in Niemann-Pick disease type C patients: a review, Orphanet Journal of Rare Diseases

Diagnostic workup and management of patients with suspected Niemann-Pick type C disease - Apostolos Papandreou, Paul Gissen, 2016

Niemann Pick Disease - an overview

National Niemann-Pick Disease Foundation, Inc. - October is Global

Experimental treatment for Niemann-Pick disease appears safe

Niemann-Pick disease type C. The diagram represents subtypes and

The Importance of Newborn Screening for Niemann-Pick Disease – NNPDF

Niemann-Pick Disease, A Pipeline Analysis Report 2018

Gene therapy shows promise for treating Niemann-Pick disease type